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Muscular Atrophy - 48 Studies Found
Estado | Estudiar |
Active, not recruiting |
Nombre del estudio: A Study to Assess the Efficacy, Safety and Pharmacokinetics of Nusinersen (ISIS 396443) in Infants With Spinal Muscular Atrophy (SMA) Condición: Spinal Muscular Atrophy Fecha: 2013-04-22 Intervenciones: Drug: nusinersen Administered by intrathecal (IT) injection |
Completed |
Nombre del estudio: An Open-label Safety, Tolerability, and Dose-range Finding Study of Nusinersen (ISIS 396443) in Participants With Spinal Muscular Atrophy (SMA) Condición: Spinal Muscular Atrophy Fecha: 2011-12-13 Intervenciones: Drug: nusinersen Administered by intrathecal (IT) injection |
Completed |
Nombre del estudio: A Study to Assess the Efficacy and Safety of Nusinersen (ISIS 396443) in Participants With Later-onset Spinal Muscular Atrophy (SMA) Condición: Spinal Muscular Atrophy Fecha: 2014-11-12 Intervenciones:
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Completed |
Nombre del estudio: A Trial of Hydroxyurea in Spinal Muscular Atrophy Condición: Spinal Muscular Atrophy Fecha: 2007-06-11 Intervenciones: Drug: Hydroxyurea |
Recruiting |
Nombre del estudio: Prospective Evaluation of Infants With Spinal Muscular Atrophy: Condición: Spinal Muscular Atrophy Fecha: 2016-07-01 |
Terminated |
Nombre del estudio: A Study of RO6885247 in Adult and Pediatric Patients With Spinal Muscular Atrophy (MOONFISH) Condición: Muscular Atrophy, Spinal Fecha: 2014-09-11 Intervenciones:
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Recruiting |
Nombre del estudio: A Study to Investigate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics and Efficacy of RO7034067 in Infants With Type1 Spinal Muscular Atrophy (Firefish) Condición: Muscular Atrophy, Spinal Fecha: 2016-09-21 Intervenciones: Drug: RO7034067 RO7034067 will be administered orally. |
Recruiting |
Nombre del estudio: A Study to Investigate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics and Efficacy of RO7034067 in Type 2 and 3 Spinal Muscular Atrophy Participants (Sunfish) Condición: Muscular Atrophy, Spinal Fecha: 2016-09-19 Intervenciones:
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Completed |
Nombre del estudio: A Pilot Therapeutic Trial Using Hydroxyurea in Type I Spinal Muscular Atrophy Patients Condición: Muscular Atrophy, Spinal Fecha: 2007-12-04 Intervenciones: Drug: Hydroxyurea |
Completed |
Nombre del estudio: A Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy Patients Condición: Muscular Atrophy, Spinal Fecha: 2007-12-04 Intervenciones: Drug: Hydroxyurea |